Using Latent Representations to Link Disjoint Longitudinal Data for Mixed-Effects Regression.
Many rare diseases offer limited established treatment options, leading patients to switch therapies when new medications emerge. To analyze the impact of such treatment switches within the low sample size limitations of rare disease trials, it is important to use all available data sources.
Many rare diseases offer limited established treatment options, leading patients to switch therapies when new medications emerge. To analyze the impact of such treatment switches within the low sample size limitations of rare disease trials, it is important to use all available data sources.
What the study was
- Study design
- Journal Article (unspecified)
- Category
- Treatment Innovation
- Maturity
- Exploratory
- Journal
- Stat Med
Why it surfaced
Matched watchlist topic 'Rare diseases with high unmet need'. Study design: Journal Article (unspecified). Score: 8/10 (N:3, R:2, D:1, P:2).
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